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![PearlF Avatar](https://lunarcrush.com/gi/w:24/cr:twitter::26368450.png) Pearl Freier [@PearlF](/creator/twitter/PearlF) on x 9335 followers
Created: 2025-07-14 19:52:07 UTC

Ultragenyx's CEO posted this comment on Linked In in response to @MPSSociety's post about the FDA rejection news re: $RARE's rare disease gene therapy for Sanfilippo Syndrome 1/n

![](https://pbs.twimg.com/media/Gv17qd8XQAA8f-0.png)

XXXXXX engagements

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**Related Topics**
[$rares](/topic/$rares)
[pearl](/topic/pearl)

[Post Link](https://x.com/PearlF/status/1944847394937692545)